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Published : February 2026

Pages : 250

Format : PDF

Delivery Time : 2-3 Business Days

Report Price : $4490.00

Monogenetic Disease Therapy Market Report 2026

Name: Monogenetic Disease Therapy Market Report 2026
Brand: The Business Research Company
Price: 4490.00 USD
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By Therapy Type (Pharmacological, Surgical, Blood Transfusion, Gene Therapies, Other Therapy Types), By Inheritance Pattern (Autosomal, Chromosomal), By Application (Cystic Fibrosis, Sickle Cell Anemia, Phenylketonuria, Other Applications), By Distribution Channel (Hospital Pharmacy, Retail Pharmacy, Online Pharmacy), By End-Users (Clinics, Hospitals, Diagnostic Centres, Home Healthcare, Other End-Users) - Market Size, Trends, And Global Forecast 2025-2034

Note that the outlook for this market is being affected by rapid changes in trade relations and tariffs globally. The report will be updated prior to delivery to reflect the latest status, including revised forecasts and quantified impact analysis. The report’s Recommendations and Conclusions sections will be updated to give strategies for entities dealing with the fast-moving international environment.

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Monogenetic Disease Therapy Market Overview

• Monogenetic Disease Therapy market size has reached to $28.3 billion in 2025

• Expected to grow to $45.58 billion in 2030 at a compound annual growth rate (CAGR) of 10%

• Growth Driver: Rising Adoption Of Precision And Personalized Medicine Is Fueling The Growth Of The Market Due To Demand For Tailored, Mutation-specific, And Highly Effective Treatments.

• Market Trend: Advancing Targeted Gene Therapy Protocols To Slow Progression Of Monogenetic Diseases

• North America was the largest region in 2025 and Asia-Pacific is the fastest growing region.

What Is Covered Under Monogenetic Disease Therapy Market?

Monogenetic disease therapy refers to advanced medical treatments developed to target diseases caused by a mutation or defect in a single gene by correcting, replacing, silencing, or compensating for the abnormal gene or its resulting protein function. These therapies include gene therapy, RNA-based treatments, enzyme replacement therapies, and targeted small-molecule drugs, all of which aim to treat the underlying genetic cause rather than only managing the clinical symptoms.

The main types of monogenetic disease therapy include pharmacological, surgical, blood transfusion, gene therapies, and other therapy types. Pharmacological therapies refer to treatments using drugs to manage symptoms or modify disease progression in patients with single-gene disorders. These therapies are classified by inheritance patterns such as autosomal and chromosomal. They are applied for diseases including cystic fibrosis, sickle cell anemia, phenylketonuria, and other applications. They are distributed through hospital pharmacies, retail pharmacies, and online pharmacies, and are used by end users including clinics, hospitals, diagnostic centres, home healthcare, and other end users.

Monogenetic Disease Therapy Market Report bar graph

What Is The Monogenetic Disease Therapy Market Size and Share 2026?

The monogenetic disease therapy market size has grown strongly in recent years. It will grow from $28.3 billion in 2025 to $31.08 billion in 2026 at a compound annual growth rate (CAGR) of 9.8%. The growth in the historic period can be attributed to human genome research progress, early gene therapy trials, rise in rare disease diagnosis, orphan drug incentives, advances in viral vectors.

What Is The Monogenetic Disease Therapy Market Growth Forecast?

The monogenetic disease therapy market size is expected to see rapid growth in the next few years. It will grow to $45.58 billion in 2030 at a compound annual growth rate (CAGR) of 10.0%. The growth in the forecast period can be attributed to growth in Gene Editing platforms, expansion of rare disease pipelines, higher genetic screening rates, increased personalized therapy funding, broader regulatory approvals. Major trends in the forecast period include single gene targeted therapies, gene replacement treatment programs, rna based genetic treatments, rare disease gene correction, precision genetic drug design.

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Global Monogenetic Disease Therapy Market Segmentation

1) By Therapy Type: Pharmacological; Surgical; Blood Transfusion; Gene Therapies; Other Therapy Types

2) By Inheritance Pattern: Autosomal; Chromosomal

3) By Application: Cystic Fibrosis; Sickle Cell Anemia; Phenylketonuria; Other Applications

4) By Distribution Channel: Hospital Pharmacy; Retail Pharmacy; Online Pharmacy

5) By End-Users: Clinics; Hospitals; Diagnostic Centres; Home Healthcare; Other End-Users

Subsegments:

1) By Pharmacological: Small Molecule Drugs; Enzyme Replacement Therapies; Protein Replacement Therapies; Immunomodulatory Drugs; Targeted Molecular Therapies

2) By Surgical: Organ Transplant Procedures; Tissue Repair Surgeries; Gene Editing Assisted Surgeries; Minimally Invasive Surgeries; Corrective Surgical Interventions

3) By Blood Transfusion: Red Blood Cell Transfusions; Platelet Transfusions; Plasma Transfusions; Stem Cell Infusions; Autologous Blood Transfusions

4) By Gene Therapies: Ex Vivo Gene Therapy; In Vivo Gene Therapy; Viral Vector Based Gene Therapy; Non Viral Vector Gene Therapy; Genome Editing Based Therapy

5) By Other Therapy Types: Cell Based Therapies; RNA Based Therapies; Protein Based Therapies; Combination Therapies; Experimental Therapies

What Is The Driver Of The Monogenetic Disease Therapy Market?

The rising adoption of precision and personalized medicine is expected to propel the growth of the monogenetic disease therapy market going forward. Precision and personalized medicine is a medical approach that tailors disease prevention, diagnosis, and treatment to an individual’s unique genetic, molecular, or lifestyle characteristics to maximize therapeutic efficacy and minimize adverse effects. The rise of precision and personalized medicine is due to healthcare providers and patients seeking tailored treatments that maximize therapeutic efficacy, minimize adverse effects, and address individual genetic, molecular, or lifestyle characteristics. Monogenetic disease therapy supports precision and personalized medicine by targeting a patient’s specific genetic mutation, enabling highly tailored and effective treatments. For instance, in February 2024, according to the Personalized Medicine Coalition, a US-based hospital and health care organization, in 2023, the FDA approved 16 new personalized treatments for rare disease patients, up from six in 2022. Therefore, the rising adoption of precision and personalized medicine is driving the growth of the monogenetic disease therapy industry.

Key Players In The Global Monogenetic Disease Therapy Market

Major companies operating in the monogenetic disease therapy market are Pfizer Inc., Sanofi S.A., Astellas Pharma Inc., Vertex Pharmaceuticals Incorporated, Sarepta Therapeutics Inc., Ptc therapeutics inc., Crispr therapeutics ag, CRISPR Therapeutics, Voyager Therapeutics Inc., Oxford Biomedica plc, REGENXBIO INC., Arcturus therapeutics holdings inc., Editas medicine Inc., American Gene Technologies, UniQure NV., MeiraGTx Limited, Prime medicine, Abeona therapeutics Inc., Blue Cross Blue Shield Association, Rocket pharmaceuticals Inc.

Global Monogenetic Disease Therapy Market Trends and Insights

Major companies operating in the monogenetic disease therapy market are focusing on developing innovative gene therapies, such as Duchenne muscular dystrophy (DMD)–targeted protocols, to slow disease progression and improve long-term patient outcomes. Duchenne muscular dystrophy–targeted protocols are structured clinical or therapeutic guidelines specifically designed to diagnose, monitor, and manage patients with Duchenne muscular dystrophy, focusing on slowing disease progression, improving muscle function, and addressing associated complications. For instance, in January 2026, Sarepta Therapeutics Inc, a US-based biopharmaceutical company, launched Elevidys for ambulatory patients aged four and older with DMD, reporting up to a 73% reduction in the rate of functional decline over three years compared with an external control group, highlighting the importance of early intervention to alter disease course and improve quality of life.

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What Are Latest Mergers And Acquisitions In The Monogenetic Disease Therapy Market?

In October 2024, Ocuphire Pharma Inc., a US-based clinical-stage ophthalmic biopharmaceutical company, acquired Opus Genetics Inc. for an undisclosed amount. With this acquisition, Ocuphire aimed to create a leading gene therapy franchise by combining its late-stage drug development expertise with Opus Genetics’ pipeline of AAV-based gene therapy candidates for conditions such as Leber congenital amaurosis and other inherited retinal disorders. Opus Genetics Inc. is a US-based clinical-stage gene therapy company specializing in monogenetic disease therapy, focused on developing AAV-based, one-time treatments for rare inherited retinal diseases caused by single-gene mutations.

Regional Insights

North America was the largest region in the monogenetic disease therapy market in 2025. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in this market report are Asia-Pacific, South East Asia, Western Europe, Eastern Europe, North America, South America, Middle East, Africa.

The countries covered in this market report are Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Taiwan, Russia, South Korea, UK, USA, Canada, Italy, Spain.

What Defines the Monogenetic Disease Therapy Market?

The monogenetic disease therapy market includes revenues earned by entities through gene replacement therapies, gene editing therapies, RNA-based therapies, cell-based gene therapies, and gene silencing or modulation therapies. The market value includes the value of related goods sold by the service provider or included within the service offering. Only goods and services traded between entities or sold to end consumers are included.

How is Market Value Defined and Measured?

The market value is defined as the revenues that enterprises gain from the sale of goods and/or services within the specified market and geography through sales, grants, or donations in terms of the currency (in USD unless otherwise specified).

The revenues for a specified geography are consumption values that are revenues generated by organizations in the specified geography within the market, irrespective of where they are produced. It does not include revenues from resales along the supply chain, either further along the supply chain or as part of other products.

What Key Data and Analysis Are Included in the Monogenetic Disease Therapy Market Report 2026?

The monogenetic disease therapy market research report is one of a series of new reports from The Business Research Company that provides market statistics, including industry global market size, regional shares, competitors with the market share, detailed market segments, market trends and opportunities, and any further data you may need to thrive in the monogenetic disease therapy industry. The market research report delivers a complete perspective of everything you need, with an in-depth analysis of the current and future state of the industry.

Author : Abhilash Pyata

Monogenetic Disease Therapy Market Report Forecast Analysis

Report Attribute	Details
Market Size Value In 2026	$31.08 billion
Revenue Forecast In 2035	$45.58 billion
Growth Rate	CAGR of 9.8% from 2026 to 2035
Base Year For Estimation	2025
Actual Estimates/Historical Data	2020-2025
Forecast Period	2026 - 2030 - 2035
Market Representation	Revenue in USD Billion and CAGR from 2026 to 2035
Segments Covered	Therapy Type, Inheritance Pattern, Application, Distribution Channel, End-Users
Regional Scope	Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East, Africa
Country Scope	The countries covered in the report are Australia, Brazil, China, France, Germany, India, ...
Key Companies Profiled	Pfizer Inc., Sanofi S.A., Astellas Pharma Inc., Vertex Pharmaceuticals Incorporated, Sarepta Therapeutics Inc., Ptc therapeutics inc., Crispr therapeutics ag, CRISPR Therapeutics, Voyager Therapeutics Inc., Oxford Biomedica plc, REGENXBIO INC., Arcturus therapeutics holdings inc., Editas medicine Inc., American Gene Technologies, UniQure NV., MeiraGTx Limited, Prime medicine, Abeona therapeutics Inc., Blue Cross Blue Shield Association, Rocket pharmaceuticals Inc.
Customization Scope	Request for Customization
Pricing And Purchase Options	Explore Purchase Options

1. Executive Summary

1.1. Key Market Insights (2020-2035)

1.2. Visual Dashboard: Market Size, Growth Rate, Hotspots

1.3. Major Factors Driving the Market

1.4. Top Three Trends Shaping the Market

2. Monogenetic Disease Therapy Market Characteristics

2.1. Market Definition & Scope

2.2. Market Segmentations

2.3. Overview of Key Products and Services

2.4. Global Monogenetic Disease Therapy Market Attractiveness Scoring And Analysis

2.4.1. Overview of Market Attractiveness Framework

2.4.2. Quantitative Scoring Methodology

2.4.3. Factor-Wise Evaluation

Growth Potential Analysis, Competitive Dynamics Assessment, Strategic Fit Assessment And Risk Profile Evaluation

2.4.4. Market Attractiveness Scoring and Interpretation

2.4.5. Strategic Implications and Recommendations

3. Monogenetic Disease Therapy Market Supply Chain Analysis

3.1. Overview of the Supply Chain and Ecosystem

3.2. List Of Key Raw Materials, Resources & Suppliers

3.3. List Of Major Distributors and Channel Partners

3.4. List Of Major End Users

4. Global Monogenetic Disease Therapy Market Trends And Strategies

4.1. Key Technologies & Future Trends

4.1.1 Biotechnology, Genomics & Precision Medicine

4.1.2 Artificial Intelligence & Autonomous Intelligence

4.1.3 Digitalization, Cloud, Big Data & Cybersecurity

4.1.4 Industry 4.0 & Intelligent Manufacturing

4.1.5 Sustainability, Climate Tech & Circular Economy

4.2. Major Trends

4.2.1 Single Gene Targeted Therapies

4.2.2 Gene Replacement Treatment Programs

4.2.3 Rna Based Genetic Treatments

4.2.4 Rare Disease Gene Correction

4.2.5 Precision Genetic Drug Design

5. Monogenetic Disease Therapy Market Analysis Of End Use Industries

5.1 Hospitals

5.2 Specialty Clinics

5.3 Diagnostic Centres

5.4 Research Hospitals

5.5 Gene Therapy Centers

6. Monogenetic Disease Therapy Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, Supply Chain Impact from Tariff War & Trade Protectionism, And Covid And Recovery On The Market

7. Global Monogenetic Disease Therapy Strategic Analysis Framework, Current Market Size, Market Comparisons And Growth Rate Analysis

7.1. Global Monogenetic Disease Therapy PESTEL Analysis (Political, Social, Technological, Environmental and Legal Factors, Drivers and Restraints)

7.2. Global Monogenetic Disease Therapy Market Size, Comparisons And Growth Rate Analysis

7.3. Global Monogenetic Disease Therapy Historic Market Size and Growth, 2020 - 2025, Value ($ Billion)

7.4. Global Monogenetic Disease Therapy Forecast Market Size and Growth, 2025 - 2030, 2035F, Value ($ Billion)

8. Global Monogenetic Disease Therapy Total Addressable Market (TAM) Analysis for the Market

8.1. Definition and Scope of Total Addressable Market (TAM)

8.2. Methodology and Assumptions

8.3. Global Total Addressable Market (TAM) Estimation

8.4. TAM vs. Current Market Size Analysis

8.5. Strategic Insights and Growth Opportunities from TAM Analysis

9. Monogenetic Disease Therapy Market Segmentation

9.1. Global Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Pharmacological, Surgical, Blood Transfusion, Gene Therapies, Other Therapy Types

9.2. Global Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Autosomal, Chromosomal

9.3. Global Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Cystic Fibrosis, Sickle Cell Anemia, Phenylketonuria, Other Applications

9.4. Global Monogenetic Disease Therapy Market, Segmentation By Distribution Channel, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Hospital Pharmacy, Retail Pharmacy, Online Pharmacy

9.5. Global Monogenetic Disease Therapy Market, Segmentation By End-Users, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Clinics, Hospitals, Diagnostic Centres, Home Healthcare, Other End-Users

9.6. Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Pharmacological, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Small Molecule Drugs, Enzyme Replacement Therapies, Protein Replacement Therapies, Immunomodulatory Drugs, Targeted Molecular Therapies

9.7. Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Surgical, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Organ Transplant Procedures, Tissue Repair Surgeries, Gene Editing Assisted Surgeries, Minimally Invasive Surgeries, Corrective Surgical Interventions

9.8. Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Blood Transfusion, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Red Blood Cell Transfusions, Platelet Transfusions, Plasma Transfusions, Stem Cell Infusions, Autologous Blood Transfusions

9.9. Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Gene Therapies, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Ex Vivo Gene Therapy, In Vivo Gene Therapy, Viral Vector Based Gene Therapy, Non Viral Vector Gene Therapy, Genome Editing Based Therapy

9.10. Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Other Therapy Types, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Cell Based Therapies, RNA Based Therapies, Protein Based Therapies, Combination Therapies, Experimental Therapies

10. Monogenetic Disease Therapy Market Regional And Country Analysis

10.1. Global Monogenetic Disease Therapy Market, Split By Region, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

10.2. Global Monogenetic Disease Therapy Market, Split By Country, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

11. Asia-Pacific Monogenetic Disease Therapy Market

11.1. Asia-Pacific Monogenetic Disease Therapy Market Overview

Region Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies

11.2. Asia-Pacific Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

12. China Monogenetic Disease Therapy Market

12.1. China Monogenetic Disease Therapy Market Overview

Country Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies

12.2. China Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

13. India Monogenetic Disease Therapy Market

13.1. India Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

14. Japan Monogenetic Disease Therapy Market

14.1. Japan Monogenetic Disease Therapy Market Overview

14.2. Japan Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

15. Australia Monogenetic Disease Therapy Market

15.1. Australia Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

16. Indonesia Monogenetic Disease Therapy Market

16.1. Indonesia Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

17. South Korea Monogenetic Disease Therapy Market

17.1. South Korea Monogenetic Disease Therapy Market Overview

17.2. South Korea Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

18. Taiwan Monogenetic Disease Therapy Market

18.1. Taiwan Monogenetic Disease Therapy Market Overview

18.2. Taiwan Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

19. South East Asia Monogenetic Disease Therapy Market

19.1. South East Asia Monogenetic Disease Therapy Market Overview

19.2. South East Asia Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

20. Western Europe Monogenetic Disease Therapy Market

20.1. Western Europe Monogenetic Disease Therapy Market Overview

20.2. Western Europe Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

21. UK Monogenetic Disease Therapy Market

21.1. UK Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

22. Germany Monogenetic Disease Therapy Market

22.1. Germany Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

23. France Monogenetic Disease Therapy Market

23.1. France Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

24. Italy Monogenetic Disease Therapy Market

24.1. Italy Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

25. Spain Monogenetic Disease Therapy Market

25.1. Spain Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

26. Eastern Europe Monogenetic Disease Therapy Market

26.1. Eastern Europe Monogenetic Disease Therapy Market Overview

26.2. Eastern Europe Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

27. Russia Monogenetic Disease Therapy Market

27.1. Russia Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

28. North America Monogenetic Disease Therapy Market

28.1. North America Monogenetic Disease Therapy Market Overview

28.2. North America Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

29. USA Monogenetic Disease Therapy Market

29.1. USA Monogenetic Disease Therapy Market Overview

29.2. USA Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

30. Canada Monogenetic Disease Therapy Market

30.1. Canada Monogenetic Disease Therapy Market Overview

30.2. Canada Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

31. South America Monogenetic Disease Therapy Market

31.1. South America Monogenetic Disease Therapy Market Overview

31.2. South America Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

32. Brazil Monogenetic Disease Therapy Market

32.1. Brazil Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

33. Middle East Monogenetic Disease Therapy Market

33.1. Middle East Monogenetic Disease Therapy Market Overview

33.2. Middle East Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

34. Africa Monogenetic Disease Therapy Market

34.1. Africa Monogenetic Disease Therapy Market Overview

34.2. Africa Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Segmentation By Inheritance Pattern, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

35. Monogenetic Disease Therapy Market Regulatory and Investment Landscape

36. Monogenetic Disease Therapy Market Competitive Landscape And Company Profiles

36.1. Monogenetic Disease Therapy Market Competitive Landscape And Market Share 2024

36.1.1. Top 10 Companies (Ranked by revenue/share)

36.2. Monogenetic Disease Therapy Market - Company Scoring Matrix

36.2.1. Market Revenues

36.2.2. Product Innovation Score

36.2.3. Brand Recognition

36.3. Monogenetic Disease Therapy Market Company Profiles

36.3.1. Pfizer Inc. Overview, Products and Services, Strategy and Financial Analysis

36.3.2. Sanofi S.A. Overview, Products and Services, Strategy and Financial Analysis

36.3.3. Astellas Pharma Inc. Overview, Products and Services, Strategy and Financial Analysis

36.3.4. Vertex Pharmaceuticals Incorporated Overview, Products and Services, Strategy and Financial Analysis

36.3.5. Sarepta Therapeutics Inc. Overview, Products and Services, Strategy and Financial Analysis

37. Monogenetic Disease Therapy Market Other Major And Innovative Companies

Ptc therapeutics inc., Crispr therapeutics ag, CRISPR Therapeutics, Voyager Therapeutics Inc., Oxford Biomedica plc, REGENXBIO INC., Arcturus therapeutics holdings inc., Editas medicine Inc., American Gene Technologies, UniQure NV., MeiraGTx Limited, Prime medicine, Abeona therapeutics Inc., Blue Cross Blue Shield Association, Rocket pharmaceuticals Inc.

38. Global Monogenetic Disease Therapy Market Competitive Benchmarking And Dashboard

39. Upcoming Startups in the Market

40. Key Mergers And Acquisitions In The Monogenetic Disease Therapy Market

41. Monogenetic Disease Therapy Market High Potential Countries, Segments and Strategies

41.1 Monogenetic Disease Therapy Market In 2030 - Countries Offering Most New Opportunities

41.2 Monogenetic Disease Therapy Market In 2030 - Segments Offering Most New Opportunities

41.3 Monogenetic Disease Therapy Market In 2030 - Growth Strategies

41.3.1 Market Trend Based Strategies

41.3.2 Competitor Strategies

42. Appendix

42.1. Abbreviations

42.2. Currencies

42.3. Historic And Forecast Inflation Rates

42.4. Research Inquiries

42.5. The Business Research Company

42.6. Copyright And Disclaimer

List Of Tables

Table 1: Global Monogenetic Disease Therapy Market, Overview Of Key Products - Product Examples

Table 2: Global Monogenetic Disease Therapy Market Attractiveness, Factor-Wise Evaluation

Table 3: Global Monogenetic Disease Therapy Market, Supply Chain Analysis

Table 4: Global Monogenetic Disease Therapy Market, Major Raw Material Providers

Table 5: Global Monogenetic Disease Therapy Market, Major Resource Providers

Table 6: Global Monogenetic Disease Therapy Market, Major Manufacturers (Suppliers)

Table 7: Global Monogenetic Disease Therapy Market, Major Distributors And Channel Partners

Table 8: Global Monogenetic Disease Therapy Market, Key Technologies & Future Trends

Table 9: Global Monogenetic Disease Therapy Market, Major Trends

Table 10: Global Monogenetic Disease Therapy Market, Major End Users

Table 11: Global Monogenetic Disease Therapy Market, PESTEL (Political, Economic, Social, Technology, Environmental and Legal) Analysis

Table 12: Global Monogenetic Disease Therapy Historic Market Growth, 2020-2025, $ Billion

Table 13: Global Monogenetic Disease Therapy Forecast Market Growth, 2025-2030F, 2035F, $ Billion

Table 14: Global Monogenetic Disease Therapy Market - TAM, US$ Billion, 2025

Table 15: Global Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 16: Global Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 17: Global Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 18: Global Monogenetic Disease Therapy Market, Segmentation By Distribution Channel, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 19: Global Monogenetic Disease Therapy Market, Segmentation By End-Users, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 20: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Pharmacological, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 21: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Surgical, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 22: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Blood Transfusion, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 23: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Gene Therapies, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 24: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Other Therapy Types, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 25: Global Monogenetic Disease Therapy Market, Split By Region, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 26: Global Monogenetic Disease Therapy Market, Split By Country, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 27: Asia-Pacific, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 28: Asia-Pacific, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 29: Asia-Pacific, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 30: China, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 31: China, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 32: China, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 33: India, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 34: India, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 35: India, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 36: Japan, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 37: Japan, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 38: Japan, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 39: Australia, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 40: Australia, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 41: Australia, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 42: Indonesia, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 43: Indonesia, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 44: Indonesia, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 45: South Korea, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 46: South Korea, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 47: South Korea, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 48: Taiwan, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 49: Taiwan, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 50: Taiwan, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 51: South East Asia, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 52: South East Asia, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 53: South East Asia, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 54: Western Europe, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 55: Western Europe, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 56: Western Europe, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 57: UK, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 58: UK, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 59: UK, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 60: Germany, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 61: Germany, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 62: Germany, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 63: France, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 64: France, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 65: France, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 66: Italy, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 67: Italy, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 68: Italy, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 69: Spain, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 70: Spain, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 71: Spain, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 72: Eastern Europe, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 73: Eastern Europe, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 74: Eastern Europe, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 75: Russia, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 76: Russia, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 77: Russia, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 78: North America, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 79: North America, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 80: North America, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 81: USA, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 82: USA, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 83: USA, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 84: Canada, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 85: Canada, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 86: Canada, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 87: South America, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 88: South America, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 89: South America, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 90: Brazil, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 91: Brazil, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 92: Brazil, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 93: Middle East, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 94: Middle East, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 95: Middle East, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 96: Africa, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 97: Africa, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 98: Africa, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Table 99: Global Monogenetic Disease Therapy Key Competitor Estimated Market Shares, 2024, Percentage (%)

Table 100: Global Monogenetic Disease Therapy Market - Company Scoring Matrix

Table 101: Upcoming Startups

Table 102: Pfizer Inc. Financial Performance

Table 103: Sanofi S.A. Financial Performance

Table 104: Astellas Pharma Inc. Financial Performance

Table 105: Vertex Pharmaceuticals Incorporated Financial Performance

Table 106: Sarepta Therapeutics Inc. Financial Performance

Table 107: Global Monogenetic Disease Therapy Market, Competitive Benchmarking (In USD Billions)

Table 108: Global Monogenetic Disease Therapy Market, Competitive Dashboard

Table 109: Global Monogenetic Disease Therapy Market Size Gain ($ Billion), 2025 – 2030 By Country

Table 110: Global, Monogenetic Disease Therapy Market Size Gain ($ Billion), Segmentation By Therapy Type, 2025 – 2030

Table 111: Global, Monogenetic Disease Therapy Market Size Gain ($ Billion), Segmentation By Inheritance Pattern, 2025 – 2030

Table 112: Global, Monogenetic Disease Therapy Market Size Gain ($ Billion), Segmentation By Application, 2025 – 2030

List Of Figures

Figure 1: Global Monogenetic Disease Therapy Market, Overview Of Key Products - Product Examples

Figure 2: Global Monogenetic Disease Therapy Market Attractiveness, Factor-Wise Evaluation

Figure 3: Global Monogenetic Disease Therapy Market, Supply Chain Analysis

Figure 4: Global Monogenetic Disease Therapy Market, Major Raw Material Providers

Figure 5: Global Monogenetic Disease Therapy Market, Major Resource Providers

Figure 6: Global Monogenetic Disease Therapy Market, Major Manufacturers (Suppliers)

Figure 7: Global Monogenetic Disease Therapy Market, Major Distributors And Channel Partners

Figure 8: Global Monogenetic Disease Therapy Market, Key Technologies & Future Trends

Figure 9: Global Monogenetic Disease Therapy Market, Major Trends

Figure 10: Global Monogenetic Disease Therapy Market, Major End Users

Figure 11: Global Monogenetic Disease Therapy Market, PESTEL (Political, Economic, Social, Technology, Environmental and Legal) Analysis

Figure 12: Global Monogenetic Disease Therapy Historic Market Growth, 2020-2025, $ Billion

Figure 13: Global Monogenetic Disease Therapy Forecast Market Growth, 2025-2030F, 2035F, $ Billion

Figure 14: Global Monogenetic Disease Therapy Market - TAM, US$ Billion, 2025

Figure 15: Global Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 16: Global Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 17: Global Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 18: Global Monogenetic Disease Therapy Market, Segmentation By Distribution Channel, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 19: Global Monogenetic Disease Therapy Market, Segmentation By End-Users, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 20: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Pharmacological, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 21: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Surgical, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 22: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Blood Transfusion, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 23: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Gene Therapies, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 24: Global Monogenetic Disease Therapy Market, Sub-Segmentation Of Other Therapy Types, By Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 25: Global Monogenetic Disease Therapy Market, Split By Region, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 26: Global Monogenetic Disease Therapy Market, Split By Country, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 27: Asia-Pacific, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 28: Asia-Pacific, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 29: Asia-Pacific, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 30: China, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 31: China, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 32: China, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 33: India, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 34: India, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 35: India, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 36: Japan, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 37: Japan, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 38: Japan, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 39: Australia, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 40: Australia, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 41: Australia, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 42: Indonesia, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 43: Indonesia, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 44: Indonesia, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 45: South Korea, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 46: South Korea, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 47: South Korea, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 48: Taiwan, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 49: Taiwan, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 50: Taiwan, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 51: South East Asia, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 52: South East Asia, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 53: South East Asia, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 54: Western Europe, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 55: Western Europe, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 56: Western Europe, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 57: UK, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 58: UK, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 59: UK, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 60: Germany, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 61: Germany, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 62: Germany, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 63: France, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 64: France, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 65: France, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 66: Italy, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 67: Italy, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 68: Italy, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 69: Spain, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 70: Spain, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 71: Spain, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 72: Eastern Europe, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 73: Eastern Europe, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 74: Eastern Europe, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 75: Russia, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 76: Russia, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 77: Russia, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 78: North America, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 79: North America, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 80: North America, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 81: USA, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 82: USA, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 83: USA, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 84: Canada, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 85: Canada, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 86: Canada, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 87: South America, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 88: South America, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 89: South America, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 90: Brazil, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 91: Brazil, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 92: Brazil, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 93: Middle East, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 94: Middle East, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 95: Middle East, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 96: Africa, Monogenetic Disease Therapy Market, Segmentation By Therapy Type, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 97: Africa, Monogenetic Disease Therapy Market, Segmentation By Inheritance Pattern, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 98: Africa, Monogenetic Disease Therapy Market, Segmentation By Application, Historic and Forecast, 2020-2025, 2025-2030F, 2035F, $ Billion

Figure 99: Global Monogenetic Disease Therapy Key Competitor Estimated Market Shares, 2024, Percentage (%)

Figure 100: Global Monogenetic Disease Therapy Market - Company Scoring Matrix

Figure 101: Upcoming Startups

Figure 102: Pfizer Inc. Financial Performance

Figure 103: Sanofi S.A. Financial Performance

Figure 104: Astellas Pharma Inc. Financial Performance

Figure 105: Vertex Pharmaceuticals Incorporated Financial Performance

Figure 106: Sarepta Therapeutics Inc. Financial Performance

Figure 107: Global Monogenetic Disease Therapy Market, Competitive Benchmarking (In USD Billions)

Figure 108: Global Monogenetic Disease Therapy Market, Competitive Dashboard

Figure 109: Global Monogenetic Disease Therapy Market Size Gain ($ Billion), 2025 – 2030 By Country

Figure 110: Global, Monogenetic Disease Therapy Market Size Gain ($ Billion), Segmentation By Therapy Type, 2025 – 2030

Figure 111: Global, Monogenetic Disease Therapy Market Size Gain ($ Billion), Segmentation By Inheritance Pattern, 2025 – 2030

Figure 112: Global, Monogenetic Disease Therapy Market Size Gain ($ Billion), Segmentation By Application, 2025 – 2030

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Frequently Asked Questions

How big is the Monogenetic Disease Therapy Market?

The Monogenetic Disease Therapy market was valued at $28.3 billion in 2025, increased to $31.08 billion in 2026, and is projected to reach $45.58 billion by 2030.

What is the Monogenetic Disease Therapy market growth?

The global Monogenetic Disease Therapy market is expected to grow at a CAGR of 10.0% from 2026 to 2035 to reach $45.58 billion by 2035.

Who are the key players in Monogenetic Disease Therapy market?

Some Key Players in the Monogenetic Disease Therapy market Include, Pfizer Inc., Sanofi S.A., Astellas Pharma Inc., Vertex Pharmaceuticals Incorporated, Sarepta Therapeutics Inc., Ptc therapeutics inc., Crispr therapeutics ag, CRISPR Therapeutics, Voyager Therapeutics Inc., Oxford Biomedica plc, REGENXBIO INC., Arcturus therapeutics holdings inc., Editas medicine Inc., American Gene Technologies, UniQure NV., MeiraGTx Limited, Prime medicine, Abeona therapeutics Inc., Blue Cross Blue Shield Association, Rocket pharmaceuticals Inc. .

What is the anticipated growth trend for the Monogenetic Disease Therapy market?

Major trend in this market includes: Advancing Targeted Gene Therapy Protocols To Slow Progression Of Monogenetic Diseases. For further insights on this market. request a sample here

Which region has the most growth potential in the Monogenetic Disease Therapy market?

North America was the largest region in the monogenetic disease therapy market in 2025. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in the monogenetic disease therapy market report are Asia-Pacific, South East Asia, Western Europe, Eastern Europe, North America, South America, Middle East, Africa.